Six is Lydia’s age in years. Six is also a number of months she lived after being diagnosed with DIPG. FDA’s Project Facilitate should help kids who, like Lydia, are denied compassionate use drugs. more→
COMPASSIONATE USE (EXPANDED ACCESS) NEWS
Make compassionate use program easy to navigate
The study we co-authored identified knowledge gaps and misperceptions about the compassionate use application process among pediatric oncologists and echoes new FDA’s Expanded Access Program Report. more→
Expanded Access Summit 2.0: It’s time for solutions
Expanded Access Summit 2.0 will address some of the unanswered questions on how to make expanded access feasible. more→
“Right To Try” is law, now what? (Health Affairs blog)
The primary obstacle encountered by patients – companies’ denials of requests – remains. more→
The ‘cruel joke’ of compassionate use and right to try: Pharma companies don’t have to comply (STAT News)
A father’s account of an attempt to get medicine for his child. more→
Right to Try does not make compassionate use access easier
The new law doesn’t change a fundamental reality about compassionate use: the biggest hurdle is persuading a drug company to agree to provide access. more→
Our abstract at 2018 ASCO annual meeting: Pediatric oncologists’ experiences with compassionate use
The lack of knowledge and paucity of support in the application process are immediate actionable barriers to wider utilization of compassionate use in pediatric oncology. more→
How to try an experimental drug when you don’t qualify for a clinical trial (Forbes)
How to handle compassionate use requests is not taught in medical school. In essence, the process has four steps. more→
To speed access to compassionate use, look beyond the FDA (Health Affairs Blog)
Contrary to widespread industry concerns that serious adverse events in a compassionate use program will lead to problems with the FDA, analysis of years of data does not show this to be the case. more→
Senate passes F.D.A. funding and ‘Right to Try’ drug bills (New York Times)
The FDA bill includes new requirements that could increase the number of cancer drugs for children. more→
Senate passes ‘right to try’ bill to help terminally ill patients get experimental drugs (Washington Post)
The Senate on August 3 passed a measure designed to make it easier for terminally ill patients to get access to experimental treatments without oversight from the FDA. more→
Nature supports RACE for Children Act
Kids v Cancer welcomes NATURE’s editorial in support of the RACE for Children Act to champion the development of promising cancer drugs for children. more→
Fairer way to distribute last-ditch drugs gets real-world trial (Nature Magazine)
Drug companies’ compassionate policies hard to decipher, and experts are testing what they hope is a fairer system to distribute drugs. more→
FDA simplifies compassionate use application and drug costs (Medscape)
As promised, the FDA has simplified the form physicians use to request investigational compassionate use drugs when all other options have been exhausted. more→
Compassionate Use Navigator addresses challenges and facilitates access to investigational drugs for pediatric oncologists (Proceedings: AACR 107th Annual Meeting 2016)
Proceedings: AACR 107th Annual Meeting 2016; April 16-20, 2016; New Orleans, LA Elena Gerasimov, Lindy Zhang, Scott Moerdler, Michael Roth, Nancy Goodman more→